Clinical Trials

We conduct clinical trials to evaluate the safety, efficacy and risk / benefit profile of investigational medical products in development. We conduct clinical trials in various regulatory jurisdictions (US, UK, EU, and other countries) based on our clinical development plans.

View our ongoing hemophilia b trials and other clinical research for our Hemophilia Program:

View our clinical trials for our LockBody Program:

For additional detail, please visit www.clinicaltrials.gov (US), www.clinicaltrialsregister.eu (EU), or registries in other jurisdictions.

View our Expanded Access Policy for investigational medical products.

Note: These compounds and their uses are investigational and have not been approved by the U.S. Food and Drug Administration or the European Medicines Agency or other regulators.

This information is only for purposes of providing a general overview of clinical trials and should not be construed as a recommendation for use of any product for unapproved uses.

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